Rare Disease Impact Report: Insights from patients and the medical community April 2013 This report was commissioned by Shire Human Genetic Therapies and developed in collaboration…

1. How can things change? By implementing a comprehensive approach to rare diseases By developing appropriate public health policies By increasing international cooperation…

1. Apps for Rare & Neglected Diseases Sean EkinsCollaborative Drug Discovery, Inc 2. Problems can be opportunities• Smaller research communities• Less investment…

Slide 1PDUFA Legislative Update NORD Corporate Council Annual Meeting Paul Kim, Foley Hoag LLP May 15 2012 Slide 2 NORD Corporate Council | 2 Current Situation Overview of…

1. Rare Disease Day: Raising Awareness, Sparking Action Path of the Blue Eye ProjectCasual Conversation Webinar 4 March 12, 2010 2. OverviewWhat is theRare Diseases Path?…

Slide 1 Taking society into account when planning HTA 1 November 2012 Bulgarian Parliament Slide 2 My intervention will cover HTA in Europe – a very brief trends overview…

eurordis.org Becoming MeMber of eurordis a the european organisation for rare Diseases 2 eurordis is the voice of rare disease patients in europe. We federate over 500 patient…