Slide 1 Phenylketonuria (PKU) TAM NGUYEN CHEM 4700 Slide 2 Introduction PKU is a common inborn metabolic disorder caused by a deficiency of the liver enzyme phenylalanine…
PowerPoint Presentation Advances in gene therapy for phenylketonuria (PKU) Cary O. Harding, MD Department of Molecular & Medical Genetics 1 Disclosures BioMarin Corporation…
PowerPoint Presentation Advances in gene therapy for phenylketonuria (PKU) Cary O. Harding, MD Department of Molecular & Medical Genetics 1 Disclosures BioMarin Corporation…