1. Why There Needs to be Open Data for Ultra-Rare and Rare Disease Drug Discovery Sean Ekins1, Alex M. Clark2, Jill Wood3,4, Lori Sames5,6 and Allison Moore7 1Collaborations…
Slide 1 1 Rare Diseases and Orphan Medicinal Products Máster en diagnóstico y terapia de las enfermedades raras Josep Torrent-Farnell Universitat Autònoma de Barcelona…