Health & Medicine Rare Dis 09

1. Implication of NGO^s in education of patients with rare diseases and general population Mihai Gafencu, MD, PhD, Save the Children - Romania 2. Introduction In the absence…

Documents First In Human Pediatric Trials and Safety Assessment for Rare and Orphan Diseases Andrew E....

First In Human Pediatric Trials and Safety Assessment for Rare and Orphan Diseases Andrew E. Mulberg, MD, FAAP Division Deputy Director OND/ODE3/DGIEP FDA Partnership is…